Global Rare Diseases Therapeutic Area Head, LSDs and Cablivi
$293.25k - $423.58kBiopharma Careers
Job Title: Global Rare Diseases Therapeutic Area Head, LSDs and Cablivi Location: Cambridge, MA About the Job Join the team transforming care for people with immune challenges, rare diseases, cancers, and neurological conditions. In Specialty Care, you’ll help deliver breakthrough treatments that bring hope to patients with some of the highest unmet needs. Reporting to the Global Head of Rare Diseases and as a member of the Global Rare Diseases Franchise Leadership Team (GRDLT), Global Rare Diseases TA Head, LSDs and Cablivi has the responsibility to manage Sanofi’s LSD portfolio and Cablivi globally in coordination with markets and global functions. Key Assets: Fabrazyme, Cerezyme, Cerdelga, venglustat (GD3 and Fabry), Xenpozyme , Myozyme, Nexviazyme, Aldurazyme and Cablivi. We are an innovative global healthcare company, committed to transforming the lives of people with immune challenges, rare diseases and blood disorders, cancers, and neurological disorders. From R&D to sales, our talented teams work together, revolutionizing treatment, continually improving products, understanding unmet needs, and connecting communities. We chase the miracles of science every single day, pursuing progress to make a real impact on millions of patients around the world. About Sanofi We’re an R&D-driven, AI-powered biopharma company committed to improving people’s lives and delivering compelling growth. Our deep understanding of the immune system – and innovative pipeline – enables us to invent medicines and vaccines that treat and protect millions of people around the world. Together, we chase the miracles of science to improve people’s lives. Main Responsibilities: Drive Global P&L accountability and lead strategic and financial planning for brands, developing sales and expense forecasts to maximize portfolio value Define and drive brand strategies for the LSds+ Cablivi portfolio, positioning Sanofi as the leader in LSDs and TTP / Rare disease space across key markets globally Lead the global launch of venglustat in GD3 and Fabry working global functions and in-country teams ensuring execution that maximizes the global strategy to defend and grow our Gaucher and Fabry businesses. Execute the co-positioning narrative for Gaucher and Fabry to maximize value for Sanofi Continue to transform and modernize our LSD business by ensuring global OPEX in-line with brand spending guidelines, go-to-market models are optimized, and content generation is 100% AI-generated Lead all supply and demand discussions with M&S and cross functionally ensuring continuity of care for all patients and avoiding stockout risk Direct all portfolio-level, cross-LSD market shaping, Find , Treat and Maintain LSDs by creating new roles with new perspectives on the team Continue to grow Cablivi in aTTP focusing on patient find initiatives in the key countries Prepare IR for earnings calls by providing clear business updates along with the LSD narrative that captures the opportunities and challenges surrounding the portfolio Build and develop a best-in‑class team with a winning culture, and foster strong cross‑functional collaboration across the organization Act as a member of the Global Rare Diseases Leadership Team and demonstrate enterprise leadership by sharing best practices, mentoring talent, contributing to franchise‑level initiatives and events About You Experience & Qualifications : A minimum of a Bachelor’s Degree is required. MBA, MS or PhD in life science is preferred Extensive and diverse industry experience: A minimum of 15 years of experience in the pharmaceutical industry, across various functions (e.g., sales, marketing, MA, BD, NPP, etc.), including in US/key markets Leadership and brand management: experience in leading teams and brand/portfolio strategies in US/key markets is required Current or prior experience managing global brands is preferred Launch and pre-launch experience: strong track record in successfully launching and pre-launching products in US/key markets is required Strong credibility in P&L management Cross-functional enterprise leadership and strong capacity to drive decision‑making with key internal stakeholders is require Stakeholder engagement: ability to advocate for Sanofi’s vision, and negotiate and drive value from key partnerships, such as alliances, analysts and the investment community, patient organizations, and scientific institutions is required) Demonstrated ability to work collaboratively in a matrixed environment with many cross-functional partners including marketing brand teams, market research, market access, medical affairs, business development, regulatory, research & development, manufacturing, finance and legal Ability to work in a fast‑paced environment and quickly adjust to changing priorities is essential Excellent interpersonal, oral and written communication skills, including ability to synthesize and deliver a clear overview of the strategy, opportunity and risks for Sanofi executives This position may require up to 25% overall travel Valid passport and ability to travel internationally Why Choose Us? Bring the miracles of science to life alongside a supportive, future-focused team. Discover endless opportunities to grow your talent and drive your career, whether it’s through a promotion or lateral move, at home or internationally. Enjoy a thoughtful, well‑crafted rewards package that recognizes your contribution and amplifies your impact. Take good care of yourself and your family, with a wide range of health and wellbeing benefits including high-quality healthcare, prevention and wellness programs and at least 14 weeks’ gender‑neutral parental leave. Sanofi US Services and its U.S. affiliates are Equal Opportunity employers committed to a culturally inclusive workforce. All qualified applicants will receive consideration for employment without regard to race; color; creed; religion; national origin; age; ancestry; nationality; marital, domestic partnership or civil union status; sex, gender, gender identity or expression; affectional or sexual orientation; disability; veteran or military status or liability for military status; domestic violence victim status; atypical cellular or blood trait; genetic information (including the refusal to submit to genetic testing) or any other characteristic protected by law. Sanofi Inc. and its U.S. affiliates are Equal Opportunity and affirmative Action employers committed to a culturally inclusive and diverse workforce. All qualified applicants will receive consideration for employment without regard to race; color; creed; religion; national origin; age; ancestry; nationality; natural or protective hairstyles; marital, domestic partnership or civil union status; sex, gender, gender identity or expression; affectional or sexual orientation; disability; veteran or military status or liability for military status; domestic violence victim status; atypical cellular or blood trait; genetic information (including the refusal to submit to genetic testing) or any other characteristic protected by law. US and Puerto Rico Residents Only North America Applicants Only The salary range for this position is: $293,250.00 - $423,583.33 All compensation will be determined commensurate with demonstrated experience. Employees may be eligible to participate in Company employee benefit programs. Additional benefits information can be found through the LINK . #J-18808-Ljbffr Biopharma Careers
$321k
...Accountable for end-to-end safety and benefit-risk strategy across the Therapeutic Area (TA), ensuring integrated, science-driven decision-making... ...2 development and marketed products. Defines and drives the global vision for patient safety within the TA. Serves as a senior...Suggested$140k - $150k
Territory Business Manager / Rare Disease Updated: Today Location: Boston... ...that clearly communicate therapeutic value. Using strong analytical... ...within their assigned geographic area. Participation in training... .... Join our game-changing, global company dedicated to creating...SuggestedWork at officeFlexible hoursNight shift$143.25k - $210k
Associate Director, Operations, Rare Disease Business Unit Company: Ipsen... ...Ipsen Ipsen is a mid-sized global biopharmaceutical company... ...transformative medicines in three therapeutic areas: Oncology, Rare Disease and... ...National Sales Director and Head of Thought Leader Liaisons (...SuggestedTemporary workHome officeFlexible hours$162k - $223k
...Affairs and a core member of Rare Disease LT. The role drives strategy... ...partners closely with the Head of Rare Disease and Medical... ...Medical Excellence, Operations, Global Medical, and Biogen North... ...and performance across the Therapeutic Area. The role plays an important...SuggestedTemporary workLocal area$150k - $185k
...done by having thorough product, disease state and market knowledge and... ...Responsibilities ESSENTIAL AREAS OF RESPONSIBILITY: The TBM... ...QUALIFICATIONS: Specialty/Rare Disease sales exp preferred... ...and neurological disorders. A global biopharmaceutical company, headquartered...SuggestedFull timeLive inWork at officeLocal areaShift workNight shift- ...Director to lead Medical Strategy & Operations for North America Rare Disease. This role anchors strategy with execution, coordinating governance and operating rhythms across Medical, Field, and Global teams. You will partner with leadership to deliver aligned plans,...
- ...budget management, and cross-functional alignment to advance rare disease patient access and outcomes. The role requires strong leadership... ..., and a track record of launching in complex specialty areas with a patient-centered mindset. Willingness to travel is essential...
- ...As a Cardiovascular and Metabolism (CVM) Therapeutic Area Biomarker Lead (TABL) (Director) you will lead the CVM disease area biomarker matrix team and be responsible... ...strategies in close collaboration with the BMD global organization which includes over 150 associates...Work at officeLocal areaFlexible hours
- Director - Efficacy, Therapeutic Area - Endocrine /Internal Medicine U.S. Remote, We are happy... ...more about Dechra! Dechra is a growing, global specialist within the world of veterinary... ...success criteria. Drive integration of disease biology, clinical practice and...Remote workWork from homeWorldwideFlexible hours
- ...Vice President, Therapy Area Head, Cardiorenal About the Company Innovative biopharmaceutical... ...across heart failure and fluid overload disease states. This executive role involves... ...teams, and representing programs in global regulatory interactions. The TAH will...
$176.4k - $327.6k
...5 LI-#hybrid The Strategy & Growth Therapeutic Area Strategy team for Cardio, Renal, and Metabolic... ...judgement to support the TA Strategy Head in developing a holistic Novartis TA... ...and the core Therapeutic Areas (TA) and Disease area of CRM to derive insightful and differentiating...Temporary workLocal area$167k - $300.7k
...Moderna is seeking a Director, Global Talent Acquisition Operations to... ...protein constructs that can have therapeutic activity inside and outside of cells... ..., across diverse therapeutic areas and routes of administration, for serious diseases that are not treatable today....Work at officeLocal area$178.5k - $257.83k
...treatment of Type 2 inflammatory diseases in a generation. As a first-in... ...with immune challenges, rare diseases, cancers, and Specialty... ...AsthmaAlign closely with the Global HEVA team to ensure US insights... ...colleagues from non-HEOR functional areas, including commercial, medical...Full time$215.9k - $292.1k
...world’s leading RNAi therapeutics company. Our 2030 ambition... ...role reports to the Head of Data, AI &... ...bespoke solutions for each area.• Define integration,... ...lives of people with rare and common diseases. Built on Nobel Prize... ...We're proud to be a globally recognized top...Full timeTemporary workLocal areaFlexible hours2 days per week$125.25k - $180.92k
Job Title: Area Business Manager - Dupixent - Allergy/ENT - Trenton... ...treatments for debilitating diseases that are often difficult to diagnose... ...for patients affected by rare and debilitating diseases for... ...research, collaboration with the global patient community, and with...Full timeWork at officeLocal areaRemote work$125.25k - $180.92k
Job title: Area Business Manager Oncology Mississippi Location: Cambridge, MAAbout the... ...are also a must.We are an innovative global healthcare company, committed to transforming... ...lives of people with immune challenges, rare diseases and blood disorders, cancers, and...Full timeRemote work$132.3k - $245.7k
...scientific and operational plans Lead strategic analyses to inform disease area, platform, and portfolio decisions Drive cross-functional... ...benefits and time off (health/life/disability, 401(k) with match, vacation and other leaves) #J-18808-Ljbffr Scorpion Therapeutics$164k - $199k
...accountable for planning and executing global clinical trials.Experience in... ...experience is a plusCurrent rare disease experience and/or gene... .... Most recently, Navreet was Head of Global Clinical Operations... ...Talent Management at Tessera Therapeutics, Ben leads Tessera’s talent...Contract workLocal area$109.2k - $174.6k
...standards including multiple regions in global trials Support testing clinical... ...constructs that can have therapeutic activity inside and outside of cells... ..., across diverse therapeutic areas and routes of administration, for serious diseases that are not treatable today....Work at officeLocal areaWork from home$183.8k - $248.6k
...quality learning experiences that meet global needs and drive engagement.Embed... ...About AlnylamWe are the leader in RNAi therapeutics – a revolutionary approach with the potential... ...transform the lives of people with rare and common diseases. Built on Nobel Prize-winning science...Full timeTemporary workLocal areaFlexible hours- ...drug development company focused on advancing novel therapeutics targeting retinal degenerative eye diseases with significant unmet medical needs. Our clinical pipeline... ...standards of an established specialty and rare disease organization. Key Responsibilities Recruit,...Local areaWorldwideNight shift
$225k - $245k
...possibilities. You’ll find that rare opportunity at... ...biologics for challenging diseases in the areas of hematology and oncology,... ...446) and are expanding our global presence with operations in... ...pharmacists, pharmacy and therapeutics groups, teaching institutions...Temporary workHome office$149.13k - $195k
...the power of RNA technology for human therapeutics, Ionis’ platform continues to revolutionize... ...product, specifically for an ultra-rare disease called Familial Chylomicronemia Syndrome... ...people with deep functional and therapeutic area expertise engaging effectively and...Temporary workWork at officeLocal areaRemote work$211.66k - $317.48k
...Title: Senior Director US Head of Country Operations, Study... ...transparently to regional and global COM leadership and... ...across development phases and therapeutic areas to deliver committed clinical... ...clinical trial environment, rare disease landscape, global regulatory...Hourly payTemporary workWork at officeLocal area3 days per week$132.3k - $245.7k
Job Description SummaryJob Title: Associate Director, Strategy, Oncology Disease Area#LI-OnsiteLocation: Cambridge, MA, United StatesRelocation Support: YesWhat if your strategic thinking could shape the future of oncology research? As Associate Director, Strategy, Oncology...Full time$162.57k - $243.85k
...and works in partnership with global study team, SDHCO, Dir SSU... ...Identifying performance issues and/or areas of opportunity for continuous... ...for clinical trials, and rare disease landscape* Demonstrated... ...clinical research in various therapeutic areas in the US.* Masters or...Contract workTemporary workLocal area$215k - $240k
...critical unmet needs in autoimmune diseases. Jade's lead candidate, JADE1... ...assets licensed from Paragon Therapeutics, an antibody discovery engine... ...in human single site to global (APAC, LATAM, etc.) phase 3,... ...experienceImmunology and/or rare disease trial management experienceExtensive...Remote work$143k - $210k
...Associate Director, Neuroscience Operations Ipsen is a mid-sized global biopharmaceutical company with a focus on transformative medicines in three therapeutic areas: Oncology, Rare Disease and Neuroscience. Supported by nearly 100 years of development experience,...Temporary workFlexible hours$301.8k - $408.2k
...About Alnylam We are the leader in RNAi therapeutics- a revolutionary approach with the... ...to transform the lives of people with rare and common diseases. Built on Nobel Prize‑winning science... ...to people. We’re proud to be a globally recognized top employer, where an authentic...Full timeContract workTemporary workLocal areaFlexible hours- Hemab Therapeutics is seeking a Senior Director of Clinical Operations — a high-impact leader... ...end-to-end delivery across a growing global portfolio, from first-in-human studies... ...models to keep Hemab at the forefront of rare disease trial execution Identify, select, and...Work at office
Do you want to receive more vacancies?
Subscribe and receive similar vacancies to Global Rare Diseases Therapeutic Area Head, LSDs and Cablivi. Be the first to apply!


